Enzyme replacement therapy in MPS II patients over 20years of age or older at treatment initiation: An international case series from the Hunter Outcome Survey (HOS)

6533b86dfe1ef96bd12c9363

RESEARCH PRODUCT

Enzyme replacement therapy in MPS II patients over 20years of age or older at treatment initiation: An international case series from the Hunter Outcome Survey (HOS)

David A.h. Whiteman Arvid Heiberg Christina Lampe

subject

Series (stratigraphy)medicine.medical_specialty business.industry Endocrinology Diabetes and Metabolism Enzyme replacement therapy Biochemistry Outcome (game theory)Surgery Endocrinology Internal medicine Genetics Medicine business Molecular Biology

year	journal	country	edition	language
2013-02-01	Molecular Genetics and Metabolism

https://doi.org/10.1016/j.ymgme.2012.11.269

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