Burden of disease suffered by patients with Morquio syndrome type A: results from a patient-reported outcomes survey

6533b7d0fe1ef96bd125ac59

RESEARCH PRODUCT

Burden of disease suffered by patients with Morquio syndrome type A: results from a patient-reported outcomes survey

Christian J. Hendriksz Lisa Bell Christina Lampe Mohit Jain Christine Lavery

subject

Burden of disease Morquio syndrome Pediatrics medicine.medical_specialty business.industry Endocrinology Diabetes and Metabolism medicine.disease Biochemistry Endocrinology Genetics Physical therapy Medicine business Molecular Biology

year	journal	country	edition	language
2014-02-01	Molecular Genetics and Metabolism

https://doi.org/10.1016/j.ymgme.2013.12.114

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