Reveglucosidase alfa (BMN 701), a GILT-tagged recombinant human acid alpha glucosidase (rhGAA), evaluation in late-onset Pompe disease: Preliminary clinical efficacy and safety results of an extension study (72-week results)

6533b7d9fe1ef96bd126c081

RESEARCH PRODUCT

Reveglucosidase alfa (BMN 701), a GILT-tagged recombinant human acid alpha glucosidase (rhGAA), evaluation in late-onset Pompe disease: Preliminary clinical efficacy and safety results of an extension study (72-week results)

C. Heusner W. Dummer Claude Desnuelle Richard J. Barohn Eugen Mengel Drago Bratkovic Pascal Laforêt Derralynn Hughes Ke Yang Barry J. Byrne Mark Roberts Tarekegn Hiwot

subject

Neurology business.industry Extension study Pediatrics Perinatology and Child Health Medicine Recombinant human acid alpha-glucosidase Late onset Neurology (clinical)Disease Clinical efficacy business Virology Genetics (clinical)

year	journal	country	edition	language
2015-10-01	Neuromuscular Disorders

https://doi.org/10.1016/j.nmd.2015.06.453

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