Author: C. Heusner

0000000000335755

AUTHOR

C. Heusner

Reveglucosidase alfa (BMN 701), a GILT-tagged recombinant human acid alpha glucosidase (rhGAA), evaluation in late-onset Pompe disease: Preliminary clinical efficacy and safety results of an extension study (72-week results)

research product

An international, phase 3, switchover study of reveglucosidase alfa (BMN 701) in subjects with late-onset Pompe disease

research product

PEPhysical Sciences and Engineering
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LSLife Sciences
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SHSocial Sciences and Humanities
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