An international, phase 3, switchover study of reveglucosidase alfa (BMN 701) in subjects with late-onset Pompe disease

6533b86dfe1ef96bd12c9d4c

RESEARCH PRODUCT

An international, phase 3, switchover study of reveglucosidase alfa (BMN 701) in subjects with late-onset Pompe disease

W. Dummer Eugen Mengel Peter Young Derralynn Hughes Tahseen Mozaffar Tarekegn Hiwot F. Eyskens Barry J. Byrne Mark Roberts Benedikt Schoser John T. Kissel Jeffrey Statland K. Sivakumar C. Heusner Alan Pestronk

subject

Pediatrics medicine.medical_specialty Neurology business.industry Pediatrics Perinatology and Child Health Switchover Medicine Late onset Neurology (clinical)Disease business Genetics (clinical)Surgery

year	journal	country	edition	language
2015-10-01	Neuromuscular Disorders

https://doi.org/10.1016/j.nmd.2015.06.023

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