Sub-analysis of long-term elosulfase alfa treatment outcomes in adults with Morquio syndrome type A

6533b827fe1ef96bd12859b3

RESEARCH PRODUCT

Sub-analysis of long-term elosulfase alfa treatment outcomes in adults with Morquio syndrome type A

Nathalie Guffon Simon Jones Rossella Parini Roberto Giugliani Adrian Quartel Karl-eugen Mengel Robert Matousek Elaina Jurecki Derralynn Hughes

subject

0301 basic medicine Pediatrics medicine.medical_specialty Morquio syndrome business.industry Endocrinology Diabetes and Metabolism Treatment outcome 030105 genetics & heredity medicine.disease Biochemistry Term (time)03 medical and health sciences chemistry.chemical_compound Endocrinology Elosulfase alfa chemistry Genetics medicine business Molecular Biology

year	journal	country	edition	language
2017-01-01	Molecular Genetics and Metabolism

https://doi.org/10.1016/j.ymgme.2016.11.157

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