Clinical outcomes of Hurler syndrome treated exclusively with enzyme replacement therapy from a young age

6533b82efe1ef96bd12930f8

RESEARCH PRODUCT

Clinical outcomes of Hurler syndrome treated exclusively with enzyme replacement therapy from a young age

Victor Kovac Kathleen R. Delaney Kyle Rudser Julie B. Eisengart Seyfullah Goekce Simon Jones Karl-eugen Mengel Jean Mercer Ans T. Van Der Ploeg Alia Ahmed Elsa Shapiro Chester B. Whitley

subject

Pediatrics medicine.medical_specialty business.industry Endocrinology Diabetes and Metabolism Enzyme replacement therapy medicine.disease Biochemistry Young age Endocrinology Genetics medicine business Hurler syndrome Molecular Biology

year	journal	country	edition	language
2015-02-01	Molecular Genetics and Metabolism

https://doi.org/10.1016/j.ymgme.2014.12.074

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