A multi-national, randomized, double-blind, placebo-controlled study to evaluate the efficacy and safety of BMN 110 treatment for mucopolysaccharidosis IVA (Morquio syndrome type A)

6533b860fe1ef96bd12c38f3

RESEARCH PRODUCT

A multi-national, randomized, double-blind, placebo-controlled study to evaluate the efficacy and safety of BMN 110 treatment for mucopolysaccharidosis IVA (Morquio syndrome type A)

Karl Eugen Mengel Simon Jones Paul Harmatz Shuan-pei Lin Thomas Fleming Roberto Giugliani Christian J. Hendriksz Vassili Valayannopoulos Derralynn Hughes Barbara K. Burton Maurizio Scarpa

subject

Morquio syndrome medicine.medical_specialty business.industry Endocrinology Diabetes and Metabolism Mucopolysaccharidosis Placebo-controlled study Physiology medicine.disease Biochemistry Double blind Endocrinology Multi national Internal medicine Genetics medicine business Molecular Biology

year	journal	country	edition	language
2013-02-01	Molecular Genetics and Metabolism

https://doi.org/10.1016/j.ymgme.2012.11.110

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