29 Clinical benefit of enzyme replacement therapy (ERT) in mucopolysaccharidosis II (MPS II, Hunter syndrome)

6533b86ffe1ef96bd12ce689

RESEARCH PRODUCT

29 Clinical benefit of enzyme replacement therapy (ERT) in mucopolysaccharidosis II (MPS II, Hunter syndrome)

A. Vellodi Christine M. Eng Paul Harmatz Susanne Wendt Joseph Muenzer R. Giugliani Marwan Shinawi Mathias Beck Rick A. Martin A. Puga S. Vijayaraghavan Uma Ramaswami B. Ulbrich Ed Wraith M. Calikoglu M.a. Cleary

subject

medicine.medical_specialty Mucopolysaccharidosis II business.industry Endocrinology Diabetes and Metabolism Hunter syndrome Enzyme replacement therapy medicine.disease Biochemistry Gastroenterology Endocrinology Internal medicine Genetics medicine business Molecular Biology

year	journal	country	edition	language
2007-12-01	Molecular Genetics and Metabolism

https://doi.org/10.1016/j.ymgme.2007.08.034

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