Search results for "gauche"

showing 10 items of 62 documents

Gošē slimības skrīnings pacientiem ar splenomegāliju, hepatomegāliju un trombocitopēniju

2018

Ievads. Gošē slimība ir viena no visbiežāk sastopamajām lizosomālās uzkrāšanās slimībām. Tās manifestēšanās vecuma un klīniskās ainas dažādības dēļ ir apgrūtināta slimības laicīga diagnostika. Mērķtiecīga slimības diagnostika ļautu laicīgi atpazīt skartos indivīdus un uzsākt nepieciešamo ārstēšanu, izvairoties no komplikācijām. Mērķis. Skrīnēt pacientus ar splenomegāliju, hepatomegāliju un/vai trombocitopēniju lai atklātu Gošē slimību un noteiktu tās izplatību Latvijas populācijā. Metodes. Darba ietvaros tika veikts prospektīvs pētījums, kura laikā RAKUS stacionāra LIC nodaļās tika atlasīti 100 pacienti ar splenomegāliju, hepatomegāliju un/vai trombocitopēniju. Pacientu nodotajos sausā asin…

glikocerebrozidāzetrombocitopēnijaGaucherGošēskrīningsMedicīna
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Monitorización e individualización posológica de glucocerebrosidasa en pacientes con enfermedad de Gaucher Tipo I

2018

La enfermedad de Gaucher tipo I (EG1) es una enfermedad de depósito lisosomal causada por una deficiencia de la enzima glucocerebrosidasa, cuyo tratamiento consiste en la reposición mediante la administración exógena de la enzima deficiente, denominada terapia enzimática sustitutiva(TES). Actualmente, existe una gran controversia y una elevada variabilidad en la dosificación de la TES y en los regímenes utilizados en la práctica clínica debido a la amplia variabilidad observada en la respuesta a la TES; además las modificaciones de dosis para objetivar respuesta al tratamiento se alargan entre 12-24 meses, en una terapia con un elevado impacto económico al sistema nacional de salud. Sin emb…

glucocerebrosidasaUNESCO::CIENCIAS MÉDICAS ::Farmacodinámica::Acción de los medicamentosindividualizaciónactividad enzimática:CIENCIAS MÉDICAS ::Farmacodinámica::Acción de los medicamentos [UNESCO]farmacocinéticagaucher
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De l’État de droit libéral à l’État de droit social. Critique et transformation de l’État de droit chez Hermann Heller

2019

This article analyzes the genesis and meaning of the concept of a “social rule of law” (sozialer Rechtsstaat) which Heller put forward in the particular context of The Weimar Republic. Heller was at this time one of the jurists who criticized the liberal ideal of law. He instead promoted a social conception that would take socio-economic inequalities into consideration. However, this did not imply eliminating the rule of law; it was rather a question of extending it or elevating it to a higher point – which he called “social democracy” and from 1929, “social rule of law”. In the context of the crisis of democracy, this kind of statement clearly had a political dimension.

linke JuristenWeimar Republic[SHS.DROIT]Humanities and Social Sciences/Law[SHS.DROIT] Humanities and Social Sciences/LawDemocracy theoryJuristes de gauche allemands[SHS.SCIPO] Humanities and Social Sciences/Political scienceWeimarer RepublikAllemagne République de WeimarEtat de droit et démocratie[SHS.SCIPO]Humanities and Social Sciences/Political scienceRechtsstaat und Demokratie
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Intraventrikuläre Obstruktionen bei der Dobutamin-Streßechokardiographie: Determinanten ihrer Entstehung und klinische Folgen (Dynamic intraventricul…

1997

Die Dobutamin-Stresechokardiographie (DSE) fuhrt zu einer starken Hyperkontraktilitat des Myokards bei Tachykardie und Vesodilatation. Diese Effekte konnen zu einer unphysiologischen Abnahme des endsystolischen Volumenindex (ESVI) mit Obstruktion des linksventrikularen Ausflustraktes (LVOT) fuhren. Bei 100 Patienten (Pat.), die sich einer DSE (5–40) μg/kg/min) unterzogen, wurde die kontinuierliche Dopplerregistrierung (DW-Doppler) vor Infusion und bei maximaler Herzfrequenz durchgefuhrt. Eine dynamische, spat-systolische, Flusakzeleration auf mehr als 2 Meter/Sekunde (m/s) unter maximaler Stimulation wurde als systolische Obstruktion des LVOT interpretiert. Manifestationsfaktoren systolisch…

medicine.medical_specialtyDobutamine stress echocardiographybusiness.industryVentricule gaucheInternal medicinemedicineCardiologyDobutamineCardiology and Cardiovascular MedicinebusinessSurgerymedicine.drugZeitschrift f�r Kardiologie
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Critical assessment of chitotriosidase analysis in the rational laboratory diagnosis of children with Gaucher disease and Niemann-Pick disease type A…

2006

Laboratory diagnosis of lysosomal storage disorders, especially sphingomyelinase deficiency (Niemann–Pick disease type A/B) and Niemann–Pick disease type C (NPC) can be challenging. We therefore aimed to analyse the feasibility of first-step screening with specific chitotriosidase cut-off values in children ≤ 10 years of age with visceral organomegaly (hepatomegaly, splenomegaly, or hepatosplenomegaly) in whom a storage disorder was suspected. We conducted a retrospective, cross-sectional, referral, single-centre study to assess diagnostic test properties in 106 individuals. Median chitotriosidase activity was 12 655 nmol/h per ml (interquartile range 4693–20982) in Gaucher disease (GD); 78…

medicine.medical_specialtyHepatosplenomegalyGastroenterologySensitivity and SpecificityOrganomegalyCentral nervous system diseaseDiagnosis DifferentialInterquartile rangePredictive Value of TestsInternal medicineGene DuplicationGenotypeGeneticsMedicineGlycogen storage diseaseHumansChildGenetics (clinical)Retrospective StudiesGaucher Diseasebusiness.industryInfantNiemann-Pick Disease Type CNiemann-Pick Disease Type BNiemann-Pick Disease Type Amedicine.diseaseEndocrinologyHexosaminidasesChemistry ClinicalChild Preschoolmedicine.symptomDifferential diagnosisbusinessNiemann–Pick diseaseJournal of inherited metabolic disease
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Retrospective Analysis of Whole-Body Magnetic Resonance Imaging of Bone Manifestations in Long-Term Treated Patients with Gaucher Disease Type 1

2018

We retrospectively assessed bone and visceral manifestations in patients with Gaucher disease type 1 (GD1) with whole-body magnetic resonance imaging (WB-MRI) to determine the effects of different timing in initiating long-term enzyme replacement therapy.In 17 patients with GD1, we performed 2 WB-MRI examinations at a median interval of 13 months. Patients had received enzyme replacement therapy with alglucerase/imiglucerase for a median of 13 years prior to the first examination. MRI results were retrospectively stratified based on treatment initiation into 2 groups: "early" (age ≤12 years, median 5 years) and "late" (during adulthood, median 32 years). We evaluated occurrence of irreversi…

medicine.medical_specialtyImiglucerase030232 urology & nephrologyDiseaseSeverity of Illness Index03 medical and health sciences0302 clinical medicineBone MarrowAlglucerase030225 pediatricsmedicineRetrospective analysisHumansEnzyme Replacement TherapyWhole Body ImagingRetrospective StudiesGaucher Diseasemedicine.diagnostic_testbusiness.industryOsteonecrosisMagnetic resonance imagingRetrospective cohort studyEnzyme replacement therapyMagnetic Resonance ImagingRecombinant ProteinsSurgeryTreatment OutcomePediatrics Perinatology and Child HealthGlucosylceramidaseWhole bodybusinessmedicine.drugKlinische Pädiatrie
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Les sociétés secrètes sous la Monarchie constitutionnelle

2004

monarchie constitutionnelle[SHS.DROIT]Humanities and Social Sciences/Law[SHS.DROIT] Humanities and Social Sciences/Lawsociétés secrètesgauche[ SHS.DROIT ] Humanities and Social Sciences/Law
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Les gauches, l'antifascisme et le pacifisme dans les années 1930

2004

pacifisme[SHS.DROIT]Humanities and Social Sciences/Law[SHS.DROIT] Humanities and Social Sciences/Lawgauchegauchesantifascisme[ SHS.DROIT ] Humanities and Social Sciences/Law
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Alain Damasio, Les furtifs

2019

Clamart, La Volte, 2019, 704 p.; International audience

roman et histoireextrême-gauchealtermondialisme[SHS.HIST] Humanities and Social Sciences/Historyanticipation[SHS.HIST]Humanities and Social Sciences/HistoryAlain Damasio
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Meetings & Alcôves. Gauches et Sexualités en Europe et auw Etats-Unisd depuis 1850

2004

sexualités[SHS.DROIT]Humanities and Social Sciences/Law[SHS.DROIT] Humanities and Social Sciences/Lawgauches[ SHS.DROIT ] Humanities and Social Sciences/Law
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