Burden of disease in patients with Morquio A syndrome: results from an international patient-reported outcomes survey

6533b7d7fe1ef96bd1268f24

RESEARCH PRODUCT

Burden of disease in patients with Morquio A syndrome: results from an international patient-reported outcomes survey

Mohit Jain Christine Lavery Lisa Bell Christian Hendriksz Christina Lampe Sema Kalkan Uçar Mahmut ÇOker

subject

Adult Quality of life medicine.medical_specialty Activities of daily living Internationality Adolescent Disease Short stature chemistry.chemical_compound Wheelchair Quality of life Elosulfase alfa Medicine Humans Genetics(clinical)Pharmacology (medical)Child Genetics (clinical)Fatigue Mobility Medicine(all)Pain measurement Patient-reported outcomes business.industry Data Collection Research Mucopolysaccharidosis IV General Medicine Gait humanities EQ-5D-5L chemistry Wheelchairs Joint pain Physical therapy medicine.symptom business Morquio A syndrome

description

WOS: 000335253700001

year	journal	country	edition	language
2013-12-17	Orphanet Journal of Rare Diseases

10.1186/1750-1172-9-32 http://dx.doi.org/10.1186/1750-1172-9-32

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