Use of 2 hydroxypropyl-beta-cyclodextrin therapy in two adult Niemann Pick Type C patients

6533b85cfe1ef96bd12bc732

RESEARCH PRODUCT

Use of 2 hydroxypropyl-beta-cyclodextrin therapy in two adult Niemann Pick Type C patients

Carmen Alcalá-vicente Inmaculada Galeano María José Company-albir Eduardo López-briz Francisco Pérez-miralles Juan Eduardo Megías-vericat Bonaventura Casanova Ana García-robles María José Fernández-megía José Luis Poveda

subject

0301 basic medicine Niemann–Pick disease type C Fatal outcome business.industry Beta-Cyclodextrins Pharmacology Intrathecal medicine.disease 03 medical and health sciences 2-Hydroxypropyl-beta-cyclodextrin 030104 developmental biology 0302 clinical medicine 2 hydroxypropyl β cyclodextrin Neurology Toxicity medicine Neurology (clinical)Metabolic disease business 030217 neurology & neurosurgery

year	journal	country	edition	language
2016-07-01	Journal of the Neurological Sciences

https://doi.org/10.1016/j.jns.2016.04.048

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