Search results for "DISCOVERY"

showing 10 items of 4119 documents

Improving mRNA-Based Therapeutic Gene Delivery by Expression-Augmenting 3' UTRs Identified by Cellular Library Screening.

2019

Synthetic mRNA has emerged as a powerful tool for the transfer of genetic information, and it is being explored for a variety of therapeutic applications. Many of these applications require prolonged intracellular persistence of mRNA to improve bioavailability of the encoded protein. mRNA molecules are intrinsically unstable and their intracellular kinetics depend on the UTRs embracing the coding sequence, in particular the 3′ UTR elements. We describe here a novel and generally applicable cell-based selection process for the identification of 3′ UTRs that augment the expression of proteins encoded by synthetic mRNA. Moreover, we show, for two applications of mRNA therapeutics, namely, (1) …

Untranslated regionCellular differentiationRNA StabilityInduced Pluripotent Stem CellsBlood DonorsComputational biologyGene deliveryBiologyCancer Vaccines03 medical and health sciencesMice0302 clinical medicineDrug DiscoveryGeneticsCoding regionAnimalsHumansRNA MessengerInduced pluripotent stem cellMolecular BiologyGene3' Untranslated RegionsCells Cultured030304 developmental biologyGene LibraryPharmacology0303 health sciencesMessenger RNAMice Inbred BALB CVaccinationGene Transfer TechniquesGenetic TherapyFibroblastsCellular Reprogramming030220 oncology & carcinogenesisMolecular MedicineFemaleOriginal ArticleReprogrammingHalf-LifeMolecular therapy : the journal of the American Society of Gene Therapy
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Design of novel small molecule base-pair recognizers of toxic CUG RNA transcripts characteristics of DM1.

2020

Graphical abstract

Untranslated regioncongenital hereditary and neonatal diseases and abnormalitiesBase pairMyotonic dystrophyBiophysicsComputational biologyBase recognitionBiologyBiochemistry03 medical and health scienceschemistry.chemical_compound0302 clinical medicineStructural BiologyRNA targetingGeneticsMBNL1030304 developmental biologyComputingMethodologies_COMPUTERGRAPHICS0303 health sciencesDrug discoveryAlternative splicingRNABiological activityNon-coding RNAComputer Science Applicationschemistry030220 oncology & carcinogenesisMolecular modellingTP248.13-248.65Small moleculeBiotechnologyResearch ArticleComputational and structural biotechnology journal
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Exploring the anticancer potential of pyrazolo[1,2-a]benzo[1,2,3,4] tetrazin-3-one derivatives: The effect on apoptosis induction, cell cycle and pro…

2013

In order to investigate their anticancer potential, four new pyrazolo[1,2-a]benzo[1,2,3,4]-tetrazinone derivatives, designed through the chemometric protocol VLAK, and three of the most active compounds of the previous series have been evaluated on some cellular events including proliferation, apoptosis induction, and cell cycle. The NCI one dose (10 mu M) screening revealed that the 8,9-di-methyl derivative showed activity against Leukemia (CCRF-CEM) and Colon cancer cell line (COLO 205), reaching 81% and 45% of growth inhibition (GI), respectively. Replacement of the two methyl groups with two chlorine atoms maintained the activity toward Leukemia cell (CCRF-CEM, GI 77%) and selectively e…

VLAK protocolStereochemistryCell Survival3Cell2Pyrazolo[1Antineoplastic AgentsApoptosisCell cycleHeLachemistry.chemical_compoundStructure-Activity RelationshipPyrazolo[12-a]benzo[1234]tetrazinone VLAK protocol Anticancer agents Apoptosis inducers Cell cycleCell Line TumorDrug DiscoverymedicineHumans2-a]benzo[1EC50Cell ProliferationPharmacologybiologyDose-Response Relationship DrugMolecular StructureCell growthOrganic ChemistryApoptosis inducers4]tetrazinoneGeneral MedicineCell cyclebiology.organism_classificationmedicine.diseaseSettore CHIM/08 - Chimica FarmaceuticaLeukemiamedicine.anatomical_structurechemistryApoptosisAnticancer agentsCancer researchGrowth inhibitionHeterocyclic Compounds 3-RingHeLa Cells
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The Italian Version of the Adult Vaccine Hesitancy Scale (aVHS) for the Working-Age Population: Cross-Cultural Adaptation, Reliability, and Validity

2022

The adult Vaccine Hesitancy Scale (aVHS) is valid and reliable for evaluating attitudes toward vaccine preventable diseases (VPDs). The aim of the present study was to evaluate the cross-cultural adaptation, reliability, and validity of the Italian version of the aVHS. After cross-cultural adaptation of the aVHS, internal consistency (IC), intra-class correlation (ICC), and content validity (S-CVI) were evaluated through a survey on 160 workers. Results of the ICC were analyzed on questionnaires administered twice at a distance of two months and revealed a satisfactory reproducibility (0.87). The IC of the aVHS was assessed by the Cronbach alpha coefficient test, with a result of 0.94, demo…

Vaccine preventable diseasePharmacologySARS-CoV-2VaccinationImmunologyCOVID-19vaccination; workplace; SARS-CoV-2; vaccine hesitancy; Italy; worker; COVID-19; vaccine preventable diseaseSARS‐CoV‐2Infectious DiseasesItalyCOVID‐19Drug DiscoveryWorkerPharmacology (medical)WorkplaceVaccine hesitancyVaccines
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1H-naphtho[2,1-b]thiete and 2H-naphtho[2,3-b]thiete- synthesis and reactivity

1994

Abstract The title compounds 4 and 8 are obtained by flash vacuum pyrolysis of the corresponding hydroxymethylthionaphthols 3 and 7. Whereas 4 shows a smooth ring opening on heating, 8 is thermally stable but reacts photochemically. The different behavior is explained on the basis of an MNDO calculation. The valence isomers 4′ and 8′ represent thioquinonemethides, which are highly reactive components in [12π + 2π]cycloaddition processes (4 → 9, 10, 11; 8 → 12).

Valence (chemistry)Flash vacuum pyrolysisChemistryStereochemistryOrganic ChemistryDrug DiscoverySous videMNDOReactive componentsReactivity (chemistry)BiochemistryMedicinal chemistryCycloadditionTetrahedron Letters
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[1,2,3]Triazoloazine/(Diazomethyl)azine Valence Tautomers from 5-Azinyltetrazoles

1978

[1,2,3]Triazoloazines are formed by thermolysis of 5-azinyltetrazoles in the gasphase or in solution. Thus, 5-(2-pyridyl)tetrazole (7) and 5-(2-pyrazinyl)tetrazole (11) yield [1,2,3]triazolo[1,5-a]pyridine (9) and [1,2,3]triazolo[1,5-a]pyrazine (13), respectively, at 400°/10−3 - 10−5 Torr. 5-(2-Phenyl-4-quinazolinyl)tetrazole (15) gives 5-phenyl[1,2,3]triazolo[1,5-c]quinazoline (17) in 75% yield by heating under reflux in mesitylene solution. 2-(Diazomethyl)pyridine (8), a valence tautomer of 9, can be trapped by fumaronitrile, leading to 3-(2-pyridyl)-1, 2-cyclopropanedicarbonitrile (19). The [1,2,3]triazoloazines undergo base catalysed H/D-exchange in D2O solution.

Valence (chemistry)PyrazineStereochemistryOrganic ChemistryBiochemistryTautomerMedicinal chemistryCatalysisInorganic ChemistryAzinechemistry.chemical_compoundchemistryDrug DiscoveryPyridineQuinazolineTetrazolePhysical and Theoretical ChemistryMesityleneHelvetica Chimica Acta
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Medicinal Plants for Insomnia Related to Anxiety: An Updated Review.

2021

AbstractSleep disorders are common among the general population and can generate health problems such as insomnia and anxiety. In addition to standard drugs and psychological interventions, there are different complementary plant-based therapies used to treat insomnia and anxiety. This review aimed to find and examine the most recent research on the use of herbal medicines for treating anxiety and insomnia as compiled from clinical trials, as well as to assess the safety and efficacy of these medicines and to elucidate their possible mechanisms of action. The process entailed a search of PubMed, Scopus, and the Cochrane Library databases from 2010 to 2020. The search terms included “sleep d…

Valerianmedicine.medical_specialtyPopulationPsychological interventionPharmaceutical ScienceCochrane LibraryAnxietyAnalytical Chemistry03 medical and health sciences0302 clinical medicineSleep Initiation and Maintenance DisordersDrug DiscoveryInsomniamedicineHumanseducationPsychiatryPharmacologyeducation.field_of_studySleep disorderPlants Medicinalbiologybusiness.industryOrganic Chemistrybiology.organism_classificationmedicine.diseaseAnxiety DisordersClinical trialComplementary and alternative medicine030220 oncology & carcinogenesisMolecular MedicineAnxietymedicine.symptombusiness030217 neurology & neurosurgeryPhytotherapyPlanta medica
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Synthesis of honokiol analogues and evaluation of their modulating action on VEGF protein secretion and telomerase-related gene expressions

2017

A group of 36 biphenyl derivatives structurally related to honokiol were synthesized by means of Suzuki coupling reactions. Their cytotoxicities were evaluated and compared to that of honokiol. Some of the compounds were then evaluated for their ability to downregulate the secretion of the VEGF protein and the expression of the VEGF, hTERT, and c-Myc genes; the two latter involved in the activation of telomerase in tumoral cells. Some of the synthetized derivatives showed promising pharmacological features as they exhibited IC50 values in low micromolar range, good therapeutic margins, and a multiple mode of action on tumor cells based on the inhibition of VEGF and, at the same time, of the…

Vascular Endothelial Growth Factor A0301 basic medicineHonokiolTelomeraseAngiogenesishonokiol analoguesGene ExpressionEnzyme-Linked Immunosorbent AssayBiologytelomeraseBiochemistryLignans03 medical and health scienceschemistry.chemical_compoundangiogenesisDownregulation and upregulationDrug DiscoveryHumansSecretionTelomerase reverse transcriptaseTelomerasePharmacologyRegulation of gene expressionBiphenyl CompoundsOrganic ChemistryVEGFHEK293 Cells030104 developmental biologySecretory proteinc-MycchemistryMCF-7 CellsCancer researchMolecular Medicinegene regulationhTERTHT29 Cells
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Synthesis of Combretastatin A-4 and 3′-Aminocombretastatin A-4 derivatives with Aminoacid Containing Pendants and Study of their Interaction with Tub…

2020

Natural product combretastatin A-4 (CA-4) and its nitrogenated analogue 3&prime

Vascular Endothelial Growth Factor ACell cycle checkpoint<i>htert</i>Pharmaceutical ScienceApoptosisAnalytical Chemistrychemistry.chemical_compound0302 clinical medicineDrug DiscoveryStilbenesc-<i>myc</i>Telomerase0303 health sciences<i>vegf</i>biologyNeovascularization PathologicChemistry3′-aminocombretastatin a-4Cell cycle<i>c-Myc</i>VEGFc-MycBiochemistryChemistry (miscellaneous)030220 oncology & carcinogenesisMCF-7 CellsMolecular Medicinecytotoxicitycell cyclehTERTHT29 CellsArticleProto-Oncogene Proteins c-mycmicrotubuleslcsh:QD241-44103 medical and health sciencesStructure-Activity Relationshiplcsh:Organic chemistryMicrotubuleCell Line TumorHumansPhysical and Theoretical Chemistry030304 developmental biologyCell ProliferationCombretastatinCombretastatin A-4Cell growthOrganic ChemistryAntineoplastic Agents PhytogenicTubulintubulinCell cultureA549 Cellsbiology.proteinM Phase Cell Cycle Checkpointscombretastatin a-4Drug Screening Assays AntitumorMolecules
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Arthrinins A–D: Novel diterpenoids and further constituents from the sponge derived fungus Arthrinium sp.

2011

Bioassay-guided fractionation of a methanolic extract of the fungus Arthrinium sp., isolated from the Mediterranean sponge Geodia cydonium, afforded 10 natural products including five new diterpenoids, arthrinins A-D (1-4) and myrocin D (5). In addition, five known compounds were obtained, which included myrocin A (6), norlichexanthone (7), anomalin A (8), decarboxycitrinone (9) and 2,5-dimethyl-7-hydroxychromone (10). The structures of all isolated compounds were unambiguously elucidated based on extensive 1D and 2D NMR and HR-MS analyzes. The absolute configuration of arthrinins A-D (1-4) was established by the convenient Mosher method performed in NMR tubes and by interpretation of the R…

Vascular Endothelial Growth Factor AClinical BiochemistryPharmaceutical ScienceAntineoplastic AgentsBiochemistryMiceAscomycotaCell Line TumorNeoplasmsDrug DiscoveryAnimalsHumansMTT assayCytotoxicityProtein Kinase InhibitorsMolecular BiologyNeovascularization PathologicKinaseChemistryOrganic ChemistryTerpenoidIn vitroPoriferaEndothelial stem cellVascular endothelial growth factor ABiochemistryCell cultureMolecular MedicineDiterpenesProtein KinasesBioorganic &amp; Medicinal Chemistry
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